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Advancing thalassemia management: Insights into clinical data and disease burden

Wednesday, October 1, 2025
2:00 PM - 3:00 PM
Main Plenary Hall - Rooms 8 & 11

Overview


Sponsor: Agios
Main Plenary Hall - Rooms 8 & 11


Details

1. Dr. Kevin H.M. Kuo . Pyruvate Kinase Activation Across Hemolytic Anemias 2. Dr. Khaled M. Musallam . Thalassemia Pathophysiology and Burden of Disease 3. Dr. Kevin H.M. Kuo . Pyruvate Kinase Activation and Clinical Data in Thalassemia: ENERGIZE 4. Dr. Maria Domenica Cappellini . Pyruvate Kinase Activation and Clinical Data in Thalassemia: ENERGIZE-T 5. Dr. Sujit Sheth . Thalassemia Advocacy Advisory Council (AAC) Global Patient Survey: Methodology & Initial Key Learnings 6. Dr. Kevin H.M. Kuo . Closing Remarks and Q&A

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