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Thalassaemia: Gene Therapy

Tracks
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Friday, October 3, 2025
4:30 PM - 5:30 PM
Room 13

Overview




Chair:
Alexis Thompson
Speakers:
Janet Kwiatkowski (US) - Real World Gene Therapy Experience in Thalassemia
Josu de la Fuente (UK) - Challenges with Widespread Implementation of Gene Therapy
Room 13


Presenters

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Dr. Alexis Thompson
Hematology Division Chief
Children's Hospital Of Philadelphia

Session Chair

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Dr Janet Kwiatkowski
Director, Thalassemia Program
Children's Hospital Of Philadelphia

Real World Gene Therapy Experience in Thalassemia

Prof. Josu de la Fuente
Consultant haematologist
Imperial College Healthcare NHS Trust, St Mary’s Hospital

Challenges with Widespread Implementation of Gene Therapy

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