Basic Science: Advances in Novel Therapeutic Strategies including Gene Therapy
Tracks
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| Friday, October 3, 2025 |
| 3:00 PM - 4:00 PM |
| Room 13 |
Overview
Chair:
Bart Biemond
Speakers:
Laura Breda (US) - Advances in in-vivo gene therapy for Thalassemia and SCD
Siana Nkya (Tanzania) - Pharmacogenomics in SCD / precision medicine
Thiago Trovati Maciel (France) - Repurposing drugs for treatment of SCD – Focus on Luspatercept
Room 13
Presenters
Prof. Bart J. Biemond
Hematologist
Amsterdam UMC
Session Chair
Dr. Laura Breda
Research Associate Professor
The Children's Hospital Of Philadelphia
Advances in in-vivo gene therapy for Thalassemia and SCD
Dr. Siana Nkya
Senior Lecturer/researcher
Muhimbili University of Health and Allied Sciences
Pharmacogenomics in SCD / precision medicine
Mr. Thiago Trovati Maciel
Researcher
Institut Imagine / INSERM
Repurposing drugs for treatment of SCD – Focus on Luspatercept
