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Top Abstracts with Expert Perspective: Red Cell Disorders and Iron Deficiency/Overload

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Sunday, April 27, 2025
11:00 AM - 12:30 PM
BSH Stage (Hall 4)

Speaker

Mr Alexandros Abdel Massih
Phd Student
King's College London

Prenatal Gene Editing Tools for Sickle Cell Disease

11:00 AM - 11:15 AM
Dr Azalea Khan
Healthcare Research Scientist
Synnovis

Development of a novel test to detect hyposplenism in sickle cell disease

11:15 AM - 11:30 AM
Dr Chidambaram Sethuraman
Specialist Registrar
Sheffield Children's Hospital NHS trust

Endocrinopathies in transfusion dependant thalassemia children- East London experience

11:30 AM - 11:45 AM
Dr Noemi Roy
Consultant Haematologist
Oxford University Hospitals NHS Trust

Next generation sequencing for rare inherited anaemias: where to with variants of uncertainty significance?

11:45 AM - 12:00 PM
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Dr Austin Kulasekararaj
Consultant Haematologist
King's College Hospital

Iptacopan maintains efficacy and safety in complement inhibitor-naïve patients with paroxysmal nocturnal haemoglobinuria (PNH): APPOINT-PNH

12:00 PM - 12:15 PM
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Dr Austin Kulasekararaj
Consultant Haematologist
King's College Hospital

COMMODORE 1: Crovalimab demonstrates 2-year efficacy and safety in switch patients with paroxysmal nocturnal haemoglobinuria

12:15 PM - 12:30 PM

Chair

Sara Stuart-Smith
Haematology Consultant
King's College Hospital, Selse Hcc

 

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